Top Websites for rare diseases

kedplasma.us

Donate plasma and help create life-saving medicines.

afm-telethon.fr

Supporting research for rare disease therapies.

aleshafond.ru

Helping children with rare diseases. Fundraising and support...

cda-amc.ca

Evaluating drugs, health technologies, and systems in Canada...

osservatoriomalattierare.it

Agenzia giornalistica dedicata alle malattie rare e tumori r...

biomarin.com

Developing medicines to treat various genetic conditions and...

chiesi.com

A global pharmaceutical company focused on research and deve...

fondazionetelethon.it

Funding research for rare genetic diseases.

genedx.com

Experts in genome and exome sequencing for patients and fami...

ultomiris.com

Official patient website for Ultomiris (ravulizumab-cwvz).

alexion.com

Delivering therapies for people with rare diseases.

sobi.com

Transforming the lives of people with rare diseases.

rarediseaseadvisor.com

Rare disease news, perspectives, and information.

sophiagenetics.com

Helping clinicians generate real-time insights for patients.

insmed.com

Developing life-transforming medicines for serious and rare ...

rarechromo.org

Understanding Rare Chromosome and Gene Disorders

sarepta.com

Developing genetic medicines for rare neuromuscular diseases...

ultragenyx.com

Treatment of rare and ultrarare genetic diseases.

telethon.fr

Support research and fight rare diseases.